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2018 Advances in the Management of Rare Diseases -

The "Recent Advances in Management of Rare Disease" report has been added to's offering.

This Genetic Technology TOE depicts new life sciences trends across rare disease management through gene therapy approaches. The corresponding clinical trials scenario for lysosomal storage diseases is also depicted.

Key Topics Covered

  1. Gene Therapy for Rare Neurological Genetic Diseases
  2. Autologous Ex Vivo Gene Therapy for Neurodegenerative Disorders
  3. Orphan Drug Accelerators to Improve Rare Diseases Business Model
  4. Lentiviral Gene Therapy Solutions for Rare and Genetic Diseases
  5. Clinical Trial Analysis
  6. Key Contacts

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Editor Details

Last Updated: 19-Oct-2018