- Global Pharma News & Resources

What’s the Big Deal About Gene Therapy?

What is Gene Theraphy

Gene therapy is introduction of DNA into a patient to treat a genetic disease or a disorder. The newly inserted DNA contains a correcting gene to correct the effects of disease causing mutations. Gene therapy is promising treatment for the genetic diseases and also includes cystic fibrosis and muscular dystrophy. Gene therapy is suitable treatment for the infectious diseases, inherited disease and cancer.

Why is it Driving the Biotechnology Industry

Gene therapy has been around since the 1980s, but there has been a lot of research and work in this area since. In December 2017 the FDA approved two therapies for actual clinical use, so we're getting closer to these therapies being used in humans on a broader scale. It's taken a while because it's a very precise way of looking at medicine and  between the research dollars, time and effort required, it takes a while for a breakthrough like this to develop.

We're starting to see that diseases are being treated from where they originated, directly from the gene that's causing that abnormality. For example, there is a particular gene therapy that's been licensed in the UK used to treat a certain type of blindness and it correcting previously non-correctable blindness. How exciting is that? This is much more advanced than simply treating the symptoms of a disease

Get More Information



The growth of the gene therapy market is regulated due to various reason which includes the rapid involvement of synthetically modified gene to treat various diseases, it helps in designing the personalized medicine, rise in the research and development of the gene therapy among the others. The gene therapy requires less doses of medicines and is one time treatment, this factor is likely to show growth opportunity for gene therapy market in coming near future.

North America is anticipated to dominate the gene therapy market in the global scenario owing to various factors such as reimbursement services, technological developments in the biotechnology industry and increasing research activities. Europe is the second largest market for the gene therapy as the various innovation are being done in this region. In 2016, European Union approved Zalmoxis for the treatment of leukemia. Asia Pacific is the fastest growing region as the studies are taking rapid pace for the biotechnological industry and increase in cardiovascular disease.. Owing to these factors the market are likely to propel the growth of the market for gene therapy market in coming future.

Top 10 Companies emerging in Gene therapy Industry are -

-Sangamo Therapeutics, Inc.
-bluebird bio, Inc.
-uniQure N.V.
-AveXis, Inc.
-Solid Biosciences.
-Spark Therapeutics, Inc.



Editor Details

Related Links

Last Updated: 25-Jun-2019