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22-Oct-2019

Abeona Therapeutics Announces Presentations at the 27th European Society of Gene and Cell Therapy (ESGCT) Congress

NEW YORK and CLEVELAND, Oct. 21, 2019 (GLOBE NEWSWIRE) -- Abeona Therapeutics Inc. (Nasdaq: ABEO), a fully-integrated leader in gene and cell therapy, today announced the presentations of data from the Transpher A Study, the Company’s ongoing Phase 1/2 clinical trial evaluating ABO-102 for the treatment of Sanfilippo syndrome type A (MPS IIIA), and research updates from its library of novel AIMTM adeno-associated virus (AAV) capsids at the 27th European Society of Gene and Cell Therapy (ESGCT) Congress, to be held October 22-25, 2019 in Barcelona, Spain.  

The data will be presented as follows:

Safety, Tolerability, Biopotency and Neurocognitive Data of ABO-102 in Transpher A, an Open-Label, Multicenter, Single-Dose, Dose-Escalation, Phase 1/2 Clinical Trial in Sanfilippo Syndrome type A (Mucopolysaccharidosis IIIA)
Oral Presentation #039
Presenter: Maria Jose de Castro, M.D., Hospital Universitario Santiago de Compostela
Session 4c: Metabolic and Genetic Diseases
Date/Time: Friday, October 25, 2019, 9:00 a.m. to 11:00 a.m. CEST
Location: Room 112

Novel AAV Capsids Show Increased Evasion to Neutralizing Antibodies Against Natural Serotypes
Poster #P347
Session Title: Poster Session I
Date/Time: Wednesday, October 23, 2019, 1:00 p.m. to 3:00 p.m. CEST
Location: Multipurpose Hall

Development of an Improved Novel AAV Capsids for Intramuscular Delivery
Poster #P027
Session Title: Poster Session I
Date/Time: Wednesday, October 23, 2019, 1:00 p.m. to 3:00 p.m. CEST
Location: Multipurpose Hall

Novel AAV Capsids for Delivery to the Retina by Intravitreal Administration
Poster #P009
Session Title: Poster Session I
Date/Time: Wednesday, October 23, 2019, 1:00 p.m. to 3:00 p.m. CEST
Location: Multipurpose Hall

Development of a Novel AAV Capsid with Improved PNS Tropism for Treating Pompe Disease by Intravenous Administration
Poster #P007
Session Title: Poster Session I
Date/Time: Wednesday, October 23, 2019, 1:00 p.m. to 3:00 p.m. CEST
Location: Multipurpose Hall

About Abeona Therapeutics
Abeona Therapeutics Inc. is a clinical-stage biopharmaceutical company developing gene and cell therapies for serious diseases. The Company’s clinical programs include EB-101, its autologous, gene-corrected cell therapy for recessive dystrophic epidermolysis bullosa, as well as ABO-102 and ABO-101, novel AAV9-based gene therapies for Sanfilippo syndrome types A and B (MPS IIIA and MPS IIIB), respectively. The Company’s portfolio of AAV9-based gene therapies also features ABO-202 and ABO-201 for CLN1 disease and CLN3 disease, respectively. Its preclinical assets include ABO-401, which uses the novel AIM™ AAV vector platform to address all mutations of cystic fibrosis. Abeona has received twenty regulatory designations from the FDA and EMA for its pipeline candidates. For more information, visit www.abeonatherapeutics.com.

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Last Updated: 22-Oct-2019